News + Press

04.05.2024 |

Suppression of NF1 Nonsense Mutations by RNA-guided RNA Pseudouridylation

04.05.2024 |

NF1 Experimental Animal Models – Histopathology and Neuroanatomical Phenotyping

04.05.2024 |

NF1 Gene Rescue in Translational Animal Models – Phase B

04.05.2024 |

EV-Based Nanocarriers for NF1 Therapies

04.05.2024 |

Pre-Clinical Development of AAV9-NF1 Gene Therapy for Neurofibromatosis Type 1

04.05.2024 |

Development of a Peptide that Restores the Mutant NF1-Ras Interaction

04.05.2024 |

Novel Vectors for Gene Therapies Targeting Primary Human Schwann Cells

04.05.2024 |

Nanoparticle Delivery of Therapeutic NF1 Signaling ERPs to Schwann Cells

04.05.2024 |

Optimization of Base and Prime Editing Strategies for NF1 Therapeutics

04.05.2024 |

Optimized AAV Vectors for Therapeutic Schwann Cell Targeting in NF1