News + Press

04.05.2024 |

Testing the Efficacy of New NF1 Gene Therapy Candidates in Human Cell Types

04.05.2024 |

Exon Skipping to Treat NF1 – Phase B

04.05.2024 |

Targeted Delivery of Full Length NF1 cDNA Using Non-Viral Vectors

04.05.2024 |

Exploring Nonsense Suppression as a Treatment for NF1 – Phase B

04.05.2024 |

Disrupting FBXW11-Mediated Degradation of NF1 to Rescue Haploinsufficiency

04.05.2024 |

RAFT-Polymerized Nanoparticles for Delivery of NF1 cDNA to Schwann Cells

04.05.2024 |

Genome Editing for the Treatment of Neurofibromatosis Type I

04.05.2024 |

Evaluating a Next Generation AAV Capsid for Targeted Transduction of Schwann Cells

04.05.2024 |

Development of Targeted Gene Therapy Platform for Neurofibromatosis Type I