News + Press

04.05.2024 |

Exploring Nonsense Suppression as a Treatment for NF1 – Phase B

04.05.2024 |

Disrupting FBXW11-Mediated Degradation of NF1 to Rescue Haploinsufficiency

04.05.2024 |

RAFT-Polymerized Nanoparticles for Delivery of NF1 cDNA to Schwann Cells

04.05.2024 |

Genome Editing for the Treatment of Neurofibromatosis Type I

04.05.2024 |

Evaluating a Next Generation AAV Capsid for Targeted Transduction of Schwann Cells

04.05.2024 |

Development of Targeted Gene Therapy Platform for Neurofibromatosis Type I

04.04.2024 |

Creating NF1-CDKN2A-ATRX Models for NF1 Associated High Grade Glioma

04.04.2024 |

Targeting NF1 Mutation Glioma Oncoproteins with Peptide Centric CAR T Cells

04.04.2024 |

hiPSC Modeling of NF1 High-Grade Glioma

04.04.2024 |

Natural History of Neurofibromatosis Type 1-Associated Non-Optic Pathway Low Grade Glioma to Support the Development of Evidence-Based Criteria for Surveillance and Initiation of Treatment